IRT Laronidase ( DrugBank: Laronidase )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
19ライソゾーム病1

19. ライソゾーム病


臨床試験数 : 854 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT00638547
(ClinicalTrials.gov)
January 2, 200811/3/2008Intrathecal Enzyme Replacement for Hurler SyndromeIntrathecal Enzyme Replacement Therapy For Patients With Mucopolysaccharidosis Type I (Hurler Syndrome)Hurler SyndromeDrug: IRT LaronidaseMasonic Cancer Center, University of MinnesotaNULLCompleted6 Months3 YearsAll26Phase 1United States