Target Gene/Pathway Pathway / Gene


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No. KEGG GENES KEGG PATHWAY KEGG DRUG DrugBank 指定難病告示番号
1 SMN2 - D10881 Nusinersen 1件: 3
2 SMN2 1件: Nucleocytoplasmic transport D11406 Risdiplam 1件: 3
3 SMN2 - D12272 Branaplam 2件: 3, 8